Article Dans Une Revue Molecular Therapy Année : 2015

Repair of Rhodopsin mRNA by Spliceosome-Mediated RNA Trans -Splicing: A New Approach for Autosomal Dominant Retinitis Pigmentosa

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cea-02155559 , version 1 (13-06-2019)

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Adeline Berger, Stéphanie Lorain, Charlène Joséphine, Mélissa Desrosiers, Cécile Peccate, et al.. Repair of Rhodopsin mRNA by Spliceosome-Mediated RNA Trans -Splicing: A New Approach for Autosomal Dominant Retinitis Pigmentosa. Molecular Therapy, 2015, 23 (5), pp.918-930. ⟨10.1038/mt.2015.11⟩. ⟨cea-02155559⟩
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