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Structure: Internal structure identifier : 549932

Demonstration of prion-like properties of mutant huntingtin fibrils in both in vitro and in vivo paradigms

Maria Masnata , Giacomo Sciacca , Alexander Maxan , Luc Bousset , Hélèna Denis , et al.
Acta Neuropathologica, 2019, 137 (6), pp.981-1001. ⟨10.1007/s00401-019-01973-6⟩
Journal articles cea-02279743v1
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A phase I/II clinical trial of autologous myoblast transplantation in facioscapulohumeral muscular dystrophy

Sabrina Sacconi , Jean-Thomas Vilquin , Serge Colson , Jonathan Bocquet , Jacques Darcourt , et al.
Myology 2016, Mar 2016, Lyon, France
Conference poster hal-02394504v1