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Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Marina Cavazzana-Calvo , Emmanuel Payen , Olivier Negre , Gary Wang , Kathleen Hehir , et al.
Nature, 2010, 467 (7313), pp.318-322. ⟨10.1038/nature09328⟩
Journal articles cea-00905288v1

HSP70 sequestration by free α-globin promotes ineffective erythropoiesis in β-thalassaemia

Arlet J.B. , Ribeil J.A. , Flavia Guillem , Olivier Negre , Adonis Hazoume , et al.
Journal articles hal-01505816v1