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Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemiaNature, 2010, 467 (7313), pp.318-322. ⟨10.1038/nature09328⟩
Journal articles
cea-00905288v1
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HSP70 sequestration by free α-globin promotes ineffective erythropoiesis in β-thalassaemiaNature, 2014, ⟨10.1038/nature13614⟩
Journal articles
hal-01505816v1
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