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authFullName_s : Marina Cavazzana-Calvo

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Marina Cavazzana-Calvo , Emmanuel Payen , Olivier Negre , Gary Wang , Kathleen Hehir , et al.
Nature, 2010, 467 (7313), pp.318-322. ⟨10.1038/nature09328⟩
Journal articles cea-00905288v1
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Hematopoietic stem cell Gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

Nathalie Cartier , Salima Hacein-Bey-Abina , Cynthia C. Bartholomae , Gabor Veres , Manfred Schmidt , et al.
Science, 2009, 326 (5954), pp.818-823. ⟨10.1126/science.1171242⟩
Journal articles cea-00817492v1