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authFullName_s : Emmanuel Payen
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Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies

Kanit Bhukhai , Edouard de Dreuzy , Marie Giorgi , Charlotte Colomb , Olivier Negre , et al.
Molecular Therapy, 2018, 26 (2), pp.480 - 495. ⟨10.1016/j.ymthe.2017.10.015⟩
Journal articles inserm-01834780v1

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Marina Cavazzana-Calvo , Emmanuel Payen , Olivier Negre , Gary Wang , Kathleen Hehir , et al.
Nature, 2010, 467 (7313), pp.318-322. ⟨10.1038/nature09328⟩
Journal articles cea-00905288v1
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Gene Therapy in a Patient with Sickle Cell Disease

Jean-Antoine Ribeil , Salima Hacein-Bey-Abina , Emmanuel Payen , Alessandra Magnani , Michaela Semeraro , et al.
New England Journal of Medicine, 2017, 376 (9), pp.848 - 855. ⟨10.1056/NEJMoa1609677⟩
Journal articles inserm-01834781v1
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Innovative Therapies for Hemoglobin Disorders

Karine Sii-Felice , Olivier Negre , Christian Brendel , Alisa Tubsuwan , Eglantine Morel-À-L’huissier , et al.
Journal articles hal-02942235v1
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Hematopoietic stem cell Gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

Nathalie Cartier , Salima Hacein-Bey-Abina , Cynthia C. Bartholomae , Gabor Veres , Manfred Schmidt , et al.
Science, 2009, 326 (5954), pp.818-823. ⟨10.1126/science.1171242⟩
Journal articles cea-00817492v1
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Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles

Anne Prel , Vincent Caval , Régis Gayon , Philippe Ravassard , Christine Duthoit , et al.
Molecular Therapy - Methods and Clinical Development, 2015, 2, pp.15039. ⟨10.1038/mtm.2015.39⟩
Journal articles hal-01219159v1