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authFullName_s : Eliane Gluckman

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Marina Cavazzana-Calvo , Emmanuel Payen , Olivier Negre , Gary Wang , Kathleen Hehir , et al.
Nature, 2010, 467 (7313), pp.318-322. ⟨10.1038/nature09328⟩
Journal articles cea-00905288v1

Clonal hematopoiesis driven by chromosome 1q/MDM4 trisomy defines a canonical route toward leukemia in Fanconi anemia

Marie Sebert , Stéphanie Gachet , Thierry Leblanc , Alix Rousseau , Olivier Bluteau , et al.
Cell Stem Cell, 2023, 30 (2), pp.153-170.e9. ⟨10.1016/j.stem.2023.01.006⟩
Journal articles hal-04157812v1