@article{cavazzanacalvo:cea-00905288, TITLE = {{Transfusion independence and HMGA2 activation after gene therapy of human $\beta$-thalassaemia}}, AUTHOR = {Cavazzana-Calvo, Marina and Payen, Emmanuel and Negre, Olivier and Wang, Gary and Hehir, Kathleen and Fusil, Floriane and Down, Julian and Denaro, Maria and Brady, Troy and Westerman, Karen and Cavallesco, Resy and Gillet-Legrand, Beatrix and Caccavelli, Laure and Sgarra, Riccardo and Maouche-Chr{\'e}tien, Leila and Bernaudin, Fran{\c c}oise and Girot, Robert and Dorazio, Ronald and Mulder, Geert-Jan and Polack, Axel and Bank, Arthur and Soulier, Jean and Larghero, J{\'e}r{\^o}me and Kabbara, Nabil and Dalle, Bruno and Gourmel, Bernard and Socie, G{\'e}rard and Chr{\'e}tien, Stany and Cartier, Nathalie and Aubourg, Patrick and Fischer, Alain and Cornetta, Kenneth and Galacteros, Fr{\'e}d{\'e}ric and Beuzard, Yves and Gluckman, Eliane and Bushman, Frederick and Hacein-Bey-Abina, Salima and Leboulch, Philippe}, URL = {https://cea.hal.science/cea-00905288}, JOURNAL = {{Nature}}, PUBLISHER = {{Nature Publishing Group}}, VOLUME = {467}, NUMBER = {7313}, PAGES = {318-322}, YEAR = {2010}, DOI = {10.1038/nature09328}, HAL_ID = {cea-00905288}, HAL_VERSION = {v1}, }